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Study Shows Promise for Genetic Base Editing in Stargardt Disease
Author: Jennie Crabbe
Researchers from Switzerland’s Institute of Molecular and Clinical Ophthalmology Basel and Beam Therapeutics say they have developed a gene editing therapy that could potentially treat Stargardt disease. Their study results, published in Nature Medicine on Jan. 8, demonstrate the therapeutic use of genetic base editing. Stargardt disease is an inherited neurodegenerative disease that leads to macular degeneration and blindness due to mutations in the ABCA4 gene. It is currently untreatable. T...
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